One Type of Genetic Mutation Erased

Researchers at MIT have cured mice of a rare liver disorder caused by a single genetic mutation using a new type of gene-editing system based on bacterial proteins. The findings, described in the March 30 issue of emNature Biotechnology/em, offer the first evidence that this gene-editing technique, known as CRISPR, can reverse disease symptoms in living animals. CRISPR, which offers an easy way to snip out mutated DNA and replace it with the correct sequence, ...